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https://doi.org/10.3325/cmj.2024.65.454

Could choosing risdiplam instead of nusinersen in the treatment of type 1 spinal muscular atrophy be a huge cost-minimization opportunity?

Andrej Belančić orcid id orcid.org/0000-0001-7848-6600 ; Department of Clinical Pharmacology, Clinical Hospital Centre Rijeka, Rijeka, Croatia *
Andrea Katrin Faour ; Vancouver Coastal Health, Vancouver, BC, Canada
Elvira Meni Maria Gkrinia ; Independent Researcher, Athens, Greece
Dinko Vitezić ; Department of Clinical Pharmacology, Clinical Hospital Centre Rijeka, Rijeka, Croatia

* Corresponding author.


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Abstract

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Hrčak ID:

336581

URI

https://hrcak.srce.hr/336581

Publication date:

15.10.2024.

Visits: 365 *